Companies in the Gene therapy industry
Gene therapyName | Description | Industry | Official Website | Location | ||
|---|---|---|---|---|---|---|
A biopharmaceutical company focused on discovery and development of small-molecule drugs to treat genetic and rare diseases. | ||||||
Amicus Therapuetics is a biotechnology company developing therapies to cure rare diseases. | ||||||
Precision BioSciences is a biotechnology developing a gene editing platform for the creation of cell therapies, gene therapies, and agricultural products. | ||||||
A biotechnology that specializes in genome editing, gene therapy, cell therapy and gene regulation. | ||||||
A synthetic biology company using CRISPR to develop a portfolio of genetic medicines. | ||||||
Sarepta Therapeutics is a biopharmaceutical company founded by Marwan Fawaz in 1980 and headquartered in Cambridge, Massachusetts developing precision genetic medicines for the treatment of rare neuromuscular diseases. | ||||||
Voyager Therapeutics is a biotechnology company founded in 2014 that is headquartered in Cambridge, Massachusetts developing gene therapies to treat neurological disorders. | ||||||
A company developing gene therapies for the treatment of genetic diseases and cancer. | ||||||
CSL Behring is a biotechnology company developing biotherapies for the treatment of life-threatening medical conditions. | ||||||
Third Rock Ventures is a venture capital firm based in Boston, founded in 2007, which invests in biotechnology startups. | ||||||
Adverum is a gene therapy company committed to discovering and developing novel medicines to patients living with rare diseases and diseases of the eye. | ||||||
Catalent develops and manufactures drugs, protein-based biologics, cell and gene therapies, and consumer health products. | ||||||
SmartPharm Therapeutics is a Cambridge, MA-based gene therapy company applying the next generation of non-viral DNA and RNA technologies to treat serious human diseases. | ||||||
Integrated DNA Technologies is a Coralville, Iowa-based company founded in 1987. | ||||||
GenScript is a Piscataway, New Jersey-based company that provides products and services for biological research and drug discovery and development, such as gene synthesis and molecular engineering. | ||||||
Dyno Therapeutics is a company based in Cambridge, Massachusetts applying artificial intelligence to gene therapy, focused on adeno-associated virus capsid engineering. | ||||||
Juventas Therapeutics is a biotechnology company founded in 2007 that is headquartered in Cleveland, Ohio developing a pipeline of regenerative therapies to treat life-threatening diseases. | ||||||
OncoSenX is a spinout company of Oisin Biotechnologies, formed to develop programmable suicide gene therapy to kill cancerous cells. | ||||||
Breakout Ventures is a venture capital firm spin off of Breakout Labs specializing in investing in "hard science" companies developing products and services by combining technology, biology, materials, and energy. | ||||||
Alliance for Regenerative Medicine (ARM) is an international community of therapeutics companies, non-profit research institutes, and patient organizations advocating for regenerative medicines. | ||||||
Generation Bio is a biotechnology company that was founded in 2016 | ||||||
Orchard Therapeutics is a biotechnology company developing gene therapies for rare diseases. | ||||||
A genetic medicines company in Massachusetts that focuses on patients suffering from rare genetic diseases. | ||||||
Vor BioPharma is a biotechnology company developing hematopoietic stem cell therapy treatments for cancer. | ||||||
GentiBio, Inc. is a biotherapeutics company developing engineered regulatory T cells (Tregs) therapies for immunology. |
