Is a
Patent attributes
Patent Applicant
Current Assignee
Patent Jurisdiction
Patent Number
Patent Inventor Names
Deborah A. Kinch0
Teresa Leah Wright0
Albert Barnes Seymour0
Diana Lamppu0
Omar L. Francone0
Date of Patent
April 9, 2024
0Patent Application Number
171479740
Date Filed
January 13, 2021
0Patent Citations
...
Patent Primary Examiner
Patent abstract
Provided herein are methods of treating a subject having a disease or disorder associated with a PAH gene mutation. The methods generally comprise administering to the subject a therapeutically effective does of a recombinant adeno-associated virus (rAAV) that can express a phenylalanine hydroxylase (PAH) polypeptide in a cell and thereby restore PAH gene function in the subject.
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