Is a
Clinical Study attributes
NCT Number
Health Conditions in Trial
Trial Recruitment Size
100
Trial Sponsor
Clinical Trial Start Date
April 27, 2021
0Primary Completion Date
March 11, 2022
0Study Completion Date
March 11, 2022
0Clinical Trial Study Type
Observational0
Observational Clinical Trial Type
Cohort0
Observational Study Perspective
Other0
Participating Facility
Official Name
Natural History Study of Batten Disease0
Last Updated
April 11, 2022
0Study summary
This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective information about the motor, behavioral and functional capabilities of patients. The study initially has 2 cohorts. Cohort 1 (n ≈ 75) includes subjects with CLN6 Batten disease. Cohort 2 (n ≈ 120) includes subjects with juvenile CLN3 Batten disease. Additional cohorts for other Batten disease subtypes may be added in the future.
Timeline
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