Is a
Clinical Study attributes
NCT Number
Health Conditions in Trial
Trial Recruitment Size
560
Trial Sponsor
Clinical Trial Start Date
February 29, 2024
0Primary Completion Date
February 28, 2031
0Study Completion Date
February 28, 2031
0Clinical Trial Study Type
Interventional0
Interventional Trial Purpose
Treatment0
Intervention Type
Drug0
Interventional Trial Phase
Phase 30
Participating Facility
Official Name
A Phase 3b Open-Label Study of Long-Term Neurocognitive Outcomes in Children With Phenylketonuria Treated With Sepiapterin0
Last Updated
March 8, 2024
0Allocation Type
NA0
Intervention Model
Single Group Assignment0
Masking Type
None (Open Label)0
Other attributes
Intervention Treatment
Sepiapterin0
Study summary
The main purpose of this trial is to evaluate the long-term efficacy of sepiapterin on preserving neurocognitive functioning in children with PKU when treatment is initiated in early childhood.
Timeline
No Timeline data yet.
Further Resources
No Further Resources data yet.
