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List of products by Biomarin Pharmaceutical

List of products by Biomarin Pharmaceutical
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Products where
Product Parent Company
Name
is
Biomarin PharmaceuticalBiomarin Pharmaceutical
Name
Description
Official Website
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Product Parent Company
Aldurazyme (laronidase)
Aldurazyme (laronidase)

The first and only enzyme replacement therapy for MPS I.

biomarin.com/our-treatments/products/aldurazyme-laronidase-for-mps-i
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
Brineura (cerliponase alfa)
Brineura (cerliponase alfa)

Treatment for any form of Batten disease.

biomarin.com/our-treatments/products/brineura
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
Naglazyme (galsulfase)
Naglazyme (galsulfase)

The first and only treatment for MPS VI.

biomarin.com/our-treatments/products/naglazyme-galsulfase-for-mps-vi
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
VOXZOGO (vosoritide)
VOXZOGO (vosoritide)

Injection

biomarin.com/our-treatments/products/voxzogo
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
Vimizim (elosulfase alfa)
Vimizim (elosulfase alfa)

Treatment for Morquio A syndrome (MPS IVA).

biomarin.com/our-treatments/products/vimizim
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
PALYNZIQ (pegvaliase-pqpz) Injection
PALYNZIQ (pegvaliase-pqpz) Injection

Prescription medication used to lower blood levels of phenylalanine (Phe).

biomarin.com/our-treatments/products/palynziq/#:~:text=PALYNZIQ®%20(Pal-lin-,dL)%20on%20their%20current%20treatment.
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
Kuvan (sapropterin dihydrochloride)
Kuvan (sapropterin dihydrochloride)

The first treatment for PKU.

biomarin.com/our-treatments/products/kuvan
Medicine
Medicine
Biomarin Pharmaceutical
Biomarin Pharmaceutical
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