Name | Description | Official Website | Industry | Launch Date | Product Parent Company | ||
---|---|---|---|---|---|---|---|
The first and only enzyme replacement therapy for MPS I. | |||||||
Treatment for any form of Batten disease. | |||||||
The first and only treatment for MPS VI. | |||||||
Injection | |||||||
Treatment for Morquio A syndrome (MPS IVA). | |||||||
Prescription medication used to lower blood levels of phenylalanine (Phe). | |||||||
The first treatment for PKU. |