Is a
Clinical Study attributes
NCT Number
Trial Recruitment Size
350
Trial Sponsor
Clinical Trial Start Date
October 31, 2012
0Primary Completion Date
February 28, 2015
0Study Completion Date
May 31, 2015
0Clinical Trial Study Type
Interventional0
Interventional Trial Purpose
Treatment0
Intervention Type
Drug0
Intervention Name
EPI-743 5 mg/kg0
Placebo0
EPI-743 15 mg/kg0
Interventional Trial Phase
Phase 20
Participating Facility
Official Name
A Phase 2B Randomized, Placebo Controlled, Double Blind Clinical Trial of EPI-743 in Children With Leigh Syndrome0
Last Updated
August 31, 2020
0Allocation Type
Randomized0
Intervention Model
Crossover Assignment0
Masking Type
Quadruple0
Masked Party
Participant0
Outcomes Assessor0
Investigator0
Care Provider0
Study summary
The purpose of this study is to evaluate the effects of EPI-743 in children with Leigh syndrome on disease severity, neuromuscular function, respiratory function, disease morbidity and mortality and disease associated biomarkers.
Timeline
No Timeline data yet.
Further Resources
No Further Resources data yet.
