Golden
BioMarin

BioMarin

BioMarin is a biopharmaceutical company based in Marin County, California.

BioMarin is a biopharmaceutical company that develops therapeutics for rare genetic diseases. The company focuses on conditions that affect small patient populations, most of whom are children.



BioMarin currently manufactures seven products:

  • Palynziq (pegvaliase-pqpz) Injection self-administered enzyme substitution therapy for PKU
  • Kuvan (sapropterin dihydrochloride) Tablets for Oral Use and Powder for Oral Solution for PKU
  • Brineura (cerliponase alfa) for CLN2 Disease
  • Naglazyme (galsulfase) for MPS VI
  • Firdapse (amifampridine phosphate) (only approved in the EU) for LEMS
  • Aldurazyme (laronidase) for MPS I



Timeline

June 1, 2017

European Medicines Agency approves Brineura as a treatment for CLN2 disease

April 27, 2017

Food & Drug Administration (FDA) approves Brineura as a treatment for CLN2 disease

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Jean-Jacques Bienaimé

Chairman and CEO



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